Expensive Cystic Fibrosis Drug Now Within Reach After Dramatic Price Drop of New Generic Version

Expensive Cystic Fibrosis Drug Now Within Reach After Dramatic Price Drop of New Generic Version

– credit, National Cancer Institute A Bangladeshi pharma company will soon release a generic version of an expensive drug for cystic fibrosis that will allow hundreds of patients worldwide to access treatment. The only pharmaceutical option available for cystic fibrosis has for years been a combination treatment called ETI (elexacaftor/tezacaftor/ivacaftor) priced between $300,000 and $370,000. … Read more

Cancer-Fighting Cells Engineered Inside Patients’ Bodies Rather Than Laboratory for the First Time

Cancer-Fighting Cells Engineered Inside Patients’ Bodies Rather Than Laboratory for the First Time

Histopathological image of multiple myoloma – credit, CC 3.0. via Wikimedia Commons In a pair of groundbreaking studies, scientists replicated a time-consuming, laboratory-based, cancer therapy within myeloma patients’ own bodies. If standardized, such an advancement would allow for one of the most successful non-chemo cancer treatments to be done both faster and cheaper. CAR T-cell … Read more

Christmas ‘Miracle’ for 6-Year-Old with Leukemia Who’s Now Thriving After T-cell Therapy Instead of Chemo

Christmas ‘Miracle’ for 6-Year-Old with Leukemia Who’s Now Thriving After T-cell Therapy Instead of Chemo

Leukemia patient Bryn Ailinger – Released by Roswell Park Cancer Center Christmas 2025 is better and brighter for one family whose daughter is on the mend from a previously untreatable form of childhood cancer. Christmas 2024 saw then-5-year-old Bryn Ailinger isolated in a child cancer ward, having been diagnosed with precursor B-cell acute lymphoblastic leukemia … Read more

Patients Thought Untreatable with Rare Disease Dramatically Improve with Common Gene Therapy

Patients Thought Untreatable with Rare Disease Dramatically Improve with Common Gene Therapy

A lumbar puncture – credit, BruceBlaus CC 3.0. via Wikimedia Commons A single-dose gene replacement therapy is found to transform the capabilities for movement in children over 2 years of age and teenagers with spinal muscular atrophy, according to research published in Nature Medicine. The effects allowed these minors who could sit but not stand … Read more

Restless Legs Syndrome Linked to Parkinson’s Risk–Making it a Perfect Case for Early Treatment

Restless Legs Syndrome Linked to Parkinson’s Risk–Making it a Perfect Case for Early Treatment

Curated Lifestyle for Unsplash + South Korean scientists recently determined that patients with restless legs syndrome (RLS) showed approximately double the Parkinson’s disease incidence. If that doesn’t sound like good news, it’s because you haven’t heard what they found next. Researchers from Korea University Ansan Hospital and collaborators then found that among those RLS patients, … Read more

Exoskeleton Walker Allows Children to Take Their First Steps After Doctors Said They Couldn’t

Exoskeleton Walker Allows Children to Take Their First Steps After Doctors Said They Couldn’t

– credit, courtesy of Trexo Robotics. At a Canadian wellness center, a unique robotic exoskeleton is allowing children with developmental disorders to walk—often for the first time. The nonprofit’s Regina location is eager to get families to come by and try it out. It can be used to correct a child’s gait or help them … Read more

New Gel Regrows Dental Enamel–Which Humans Cannot Do–and Could Revolutionize Tooth Care

New Gel Regrows Dental Enamel–Which Humans Cannot Do–and Could Revolutionize Tooth Care

Electron microscopy images of a tooth with demineralized enamel (left) and a similar demineralized tooth after a 2-week treatment (right) – credit, Univ of Nottingham Chemists in England have created a gel that can repair and regenerate tooth enamel, opening up new possibilities for effective and long-lasting dental treatment. The gel can be rapidly applied … Read more