Successful World First: Baby Treated with Personalized CRISPR Gene Therapy for Rare Disease is Now ‘Thriving’

Successful World First: Baby Treated with Personalized CRISPR Gene Therapy for Rare Disease is Now ‘Thriving’

Dr. Kiran Musunru (left) and Dr. Rebecca Ahrens-Nicklas (right) led the researchers who developed a personalized treatment for baby KJ – Released CHOP and Penn CRISPR has been used to create a genetic therapy option for a child born in Pennsylvania with a rare metabolic disorder. Unable to convert ammonia to urea, newborn KJ was … Read more

Tiny ‘Pouch-Cam’ Provides Rare Glimpse of Endangered Tree Kangaroo Developing Inside its Mother (LOOK)

Tiny ‘Pouch-Cam’ Provides Rare Glimpse of Endangered Tree Kangaroo Developing Inside its Mother (LOOK)

Goodfellow’s tree kangaroo joey – SWNS / Chester Zoo Amazing “pouch cam” images provide a rare glimpse into the hidden world of an endangered baby kangaroo after he was born the size of a jellybean at a UK zoo. Experts say the special arrival marks a major conservation milestone for one of the world’s most … Read more

Tiny Baby Born With Hands Smaller Than a Fingertip is Now Home After a Year–And Developing Normally

Tiny Baby Born With Hands Smaller Than a Fingertip is Now Home After a Year–And Developing Normally

Preemie baby Gabriel Golden at Vanderbilt NICU-SWNS A premature baby, born so tiny his hand was smaller than his dad’s fingertip, is finally home and healthy after a year in the hospital. Gabriel Golden was born weighing one pound in September 2024 after just 22 weeks gestation. He endured nearly a year in the Vanderbilt … Read more

Couple Who Started IVF Last Christmas Day Welcomed a Baby After 11 Year Battle

Couple Who Started IVF Last Christmas Day Welcomed a Baby After 11 Year Battle

Helen Delgard and husband Stephane with baby Noah – family photo, via SWNS A couple who started IVF last Christmas Day has given birth to a baby boy after 11 years of trying to conceive. Helen Delgard was warned she may never be able to conceive naturally with her husband Stephane, but following a January … Read more

Boy with Rare Genetic Disorder Amazes Doctors After World-First Gene Therapy

Boy with Rare Genetic Disorder Amazes Doctors After World-First Gene Therapy

Courtesy of Oliver Chu family The first child in history has successfully been treated with a new genetic therapy for an ultra-rare developmental defect called Hunter syndrome. Several years in the making, Oliver Chu became the first in the world to receive the stem cell-based treatment in February, and 3 months later seemed to be … Read more

Exoskeleton Walker Allows Children to Take Their First Steps After Doctors Said They Couldn’t

Exoskeleton Walker Allows Children to Take Their First Steps After Doctors Said They Couldn’t

– credit, courtesy of Trexo Robotics. At a Canadian wellness center, a unique robotic exoskeleton is allowing children with developmental disorders to walk—often for the first time. The nonprofit’s Regina location is eager to get families to come by and try it out. It can be used to correct a child’s gait or help them … Read more

Baby Sea Otter Named Caterpillar Rescued off Central California Coast

Baby Sea Otter Named Caterpillar Rescued off Central California Coast

– credit, Marine Mammal Center via Instagram Conservationists recently reunited a mother otter with her baby and caught it on film. It seems surreal when marine conservationists plop the lost baby sea otter into the frigid waters of Morro Bay in Central California. Before it makes its way back into the arms of its mother, … Read more